Micropublications

DOI Case ID Clinician Title Created
View paper 9976 Dr. Sébastien KÜRY (sekury) A case of PSMC5-associated neurodevelopmental proteasomopathy 3.1.2024
View paper 10654 Ms. Julia Suh (dsuh) Case report of an adult woman with Phelan-McDermid-Syndrome 20.2.2024
View paper 13037 Dr. Sofia Douzgou Houge (SofiaDouzgou) The distinctive gestalt of the CDK13-related developmental disorder is grossly independent from ethnical variance 9.12.2024
View paper 11222 Dr. Alessandro Mauro SPINELLI (amspinelli) An adult case of Koolen-de Vries syndrome - Is post-lingual sensorineural hearing loss less infrequent than commonly assumed? 31.3.2024
View paper 11192 Dr. Miroslaw Kwasniewski (miroslawkwasniewski) Broad phenotypic spectrum of SYNGAP1-related disorder: a case with epilepsy, severe developmental delay, and atypical sensory features 28.3.2024
View paper 11195 Dr. Miroslaw Kwasniewski (miroslawkwasniewski) Atypical presentation of Glass syndrome in a child with epilepsy, autism, and unusual bleeding and thermoregulation issues 28.3.2024
View paper 11189 Dr. Karolina Chwialkowska (karolinachwialkowska) Multiple congenital anomalies-hypotonia-seizures syndrome 3 in a child with cerebellar ataxia and autism: evidence of phenotypic expansion 28.3.2024
View paper 11193 Dr. Karolina Chwialkowska (karolinachwialkowska) Hyperphosphatasia with mental retardation syndrome type 1 in a child with seizures and craniofacial anomalies 28.3.2024
View paper 11194 Dr. Karolina Chwialkowska (karolinachwialkowska) Baraitser-Winter syndrome type 1 in an infant with craniofacial dysmorphism, facial asymmetry, and sensorineural hearing loss 28.3.2024
View paper 11284 Dr. Nadja Ehmke (nadja) Severe congenital hearing loss due to a homozygous SLC26A4 splice variant 5.4.2024
View paper 15432 Ms. Beatriz de Carvalho Nunes (beacnunes) ZMYND11-related syndromic intellectual disability diagnosis in a case with classic Cornelia de Lange syndrome phenotype 5.10.2025
View paper 9953 Ms. Beatriz de Carvalho Nunes (beacnunes) Deep intronic NIPBL splice site variant in a patient with a mild presentation of classic Cornelia de Lange syndrome phenotype 3.1.2024
View paper 9932 Ms. Beatriz de Carvalho Nunes (beacnunes) Cornelia de Lange Syndrome in a woman with mild phenotype and advanced age 2.1.2024
View paper 11223 Dr. Alessandro Mauro SPINELLI (amspinelli) Clinically-mild CHD8-related neurodevelopmental disorder with overgrowth in adulthood 31.3.2024
View paper 9958 Ms. Beatriz de Carvalho Nunes (beacnunes) Classic Cornelia de Lange syndrome phenotype in a patient with a mosaic NIPBL variant absent in blood 3.1.2024
View paper 11494 Dr. Agusti Rodriguez-Palmero (arodriguezpalmero) Beyond Asymptomatic Carriers: Clinical Burden of a KDM5C Female Patient 13.5.2024
View paper 9003 Dr. Franziska Schnabel (schnabelf) ZTTK Syndrome in Early Childhood: A Case Report 2.5.2023
View paper 13098 Dr. Himanshu Goel (Himanshugoel) Multiexon SOX5 Deletion in a Male with Lamb-Shaffer Syndrome 18.12.2024
View paper 12249 Dr. Himanshu Goel (Himanshugoel) Expanding the Phenotypic Spectrum of BRSK2-Related Neurodevelopmental Disorder: A Case with Bilateral Ptosis and Dysmorphic Features 26.8.2024
View paper 14389 Dr. Himanshu Goel (Himanshugoel) Myhre syndrome due to a recurrent SMAD4 p.Arg496Cys variant in a 17-year-old boy: clinical and neuroimaging findings 18.5.2025
View paper 11137 Mr. Gaber Bergant (gbergant) Atypical Wolf–Hirschhorn Syndrome in a Boy with a Novel NSD2 Loss-of-Function Variant 26.3.2024
View paper 11140 Mr. Gaber Bergant (gbergant) Parietal foramina 2 in a 5-year-old girl with persistent open fontanels and dysmorphic features 26.3.2024
View paper 15390 Ms. Beatriz de Carvalho Nunes (beacnunes) Identification of a pathogenic variant in KAT6B in a patient with genitopatellar syndrome: A case report 30.9.2025
View paper 15389 Ms. Beatriz de Carvalho Nunes (beacnunes) Wiedemann-Steiner syndrome diagnosis in a patient with clinical suspicion of Rubinstein-Taybi syndrome 30.9.2025
View paper 11393 Dr. Nergis Güzel (neguezel) Case report of a girl with PTEN hamartoma tumor syndrome 24.4.2024
View paper 11458 Dr. Eric Olinger (eolinger) Trio exome reveals PSMC5-associated neurodevelopmental proteasomopathy in an 18-year-old male with mild ID, microcephaly, and facial dysmorphism 8.5.2024
View paper 9819 Dr. Luisa Averdunk (Luisa) SLC6A8-associated creatine transporter deficiency in a female individual with normal urine and plasma creatine metabolite levels, but a 50% reduction in the cerebral creatine peak on quantitative reanalysis of MR spectroscopy 17.11.2023
View paper 9820 Dr. Luisa Averdunk (Luisa) A case of RAI-related Smith-Magenis sydrome with obesity and small-stepped and robotic gait 17.11.2023
View paper 9822 Dr. Luisa Averdunk (Luisa) A case of SMC3-related Cornelia de Lange syndrome 17.11.2023
View paper 13108 Prof. Katrin Õunap (KatrinOunap) A case with coarse facial features, mandibular prognathia, and macrotia, in combination with neurobehavioral abnormalities and a missense variant in ABCA2 18.12.2024
View paper 14032 Dr. Clara Velmans (cvelmans) Verheij Syndrome with normal intelligence after a 10-year diagnostic odyssey 17.4.2025
View paper 14021 Dr. Clara Velmans (cvelmans) GestaltMatcher facial analysis helped confirm the diagnosis of Chung-Jansen Syndrome 16.4.2025
View paper 11041 Prof. Andreas Tzschach (tzschach) Novel ZBTB20 variant in a patient with Primrose syndrome 20.3.2024
View paper 9974 Dr. Sébastien KÜRY (sekury) A case of PSMC5-associated neurodevelopmental proteasomopathy 3.1.2024
View paper 10886 Dr. Sarah Wiethoff (SarahWiethoff) Case report of x-linked spinal and bulbar muscular atrophy with pronounced facial muscle atrophy and fasciculations 8.3.2024
View paper 7155 Dr. Ibrahim Abdelrazek (Ibrahim) Novel De Novo KMT2A Missense Variant in a Boy with Wiedemann-Steiner Syndrome 17.6.2022
View paper 7104 Dr. Ibrahim Abdelrazek (Ibrahim) Novel Homozygous SCARF2 Nonsense Variant in Two Siblings with Van den Ende-Gupta Syndrome 13.5.2022
View paper 11173 Dr. Mert Karakaya (mertk) Expanding the Clinical Presentation of Wisconsin Syndrome: A 3q24q25.3 Deletion Including ZIC1 and ZIC4 28.3.2024
View paper 15254 Dr. Ibrahim Abdelrazek (Ibrahim) A homozygous synonymous NOP58 variant associated with a novel ribosomopathy 18.9.2025
View paper 8277 Dr. Amaia Lasa-Aranzasti (lasa.aranzasti) CTNNB1 Syndrome with Spinal Lipoma: A Case Report Highlighting Medullary Involvement 21.11.2022
View paper 9315 Dr. Theresa Brunet (Theresa.Brunet) Molecular autopsy leading to the diagnosis of TBCK-associated disorder 16.6.2023
View paper 11244 Dr. Christopher CY Mak (cmakl) Novel de novo JAG1 frameshift mutation in Alagille syndrome with early liver transplant requirement 2.4.2024
View paper 9281 Dr. Miriam Elbracht (mielbracht) Case report of a girl with NEURODEVELOPMENTAL DISORDER WITH DYSMORPHIC FACIES AND DISTAL SKELETAL ANOMALIES; NEDDFSA (ZMIZ1 related) 1.6.2023
View paper 9903 Dr. Luisa Averdunk (Luisa) From Face to Function: SEC24C Deficiency Mimics GPI-Anchor Biosynthesis Disorder 19.12.2023
View paper 11221 Dr. Yuri Zarate (yzarate) SATB2-associated syndrome and a splice-site variant 31.3.2024
View paper 9660 Dr. Antonio Martinez Monseny (afmartinez) Clinical Variability in MECP2 Duplication Syndrome: Highlighting Sialorrhea as the Daily Challenge 8.9.2023
View paper 14383 Dr. Hanna Havriushenko (Hanna_Havriushenko) A familial case of KMT5B-associated autosomal dominant neurodevelopmental disorder 18.5.2025
View paper 10693 Ms. Hellen Lesmann (Hellenlesmann) Atypical presentation of a case with Noonan syndrome with multiple lentigines 22.2.2024

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